Revolutionary Gene Therapy Offers New Hope for Sickle Cell Disease Patients
New findings from a clinical trial, recently published in the New England Journal of Medicine, suggest that stem cell gene therapy could be a potential…
New findings from a clinical trial, recently published in the New England Journal of Medicine, suggest that stem cell gene therapy could be a potential…
Scientists from the Shenzhen Institute of Advanced Technology (SIAT) within the Chinese Academy of Sciences (CAS), along with their partners, have designed a targeted gene…
Guiding cells to natural target region key to functional recovery. In a new study in mice, a team of researchers from the University of California,…
Scientists at .NeuroRestore, Switzerland, report in Science that they have developed a gene therapy that was proven in mice to stimulate nerve regrowth across spinal…
An international team of researchers has developed a new method to deliver drugs into the inner ear. This breakthrough was made possible by utilizing the…
Researchers from UCL, Great Ormond Street Hospital, and the Wellcome Sanger Institute have unveiled findings that shed light on why certain children experience extended remission…
Gene Therapy for Alcohol Use Disorder Gene therapy might offer a one-time, sustained treatment for patients with serious alcohol addiction, also called alcohol use disorder,…
Researchers at The Institute of Psychiatry, Psychology & Neuroscience (IoPPN) at King’s College London have successfully reversed hearing loss in mice. Their findings, published in…
Already used to treat Parkinson’s disease, researchers found surgical treatment dramatically reduced chronic heavy drinking. A form of gene therapy currently used to treat Parkinson’s…
Scientists have pinpointed the area where a protein regulates sodium ion channels, and by inserting the channel’s genetic material into a virus, they were able…
Research study’s findings offer a potential alternative to surgical spaying. Currently, there are no contraceptives capable of producing permanent sterilization in companion animals. Spaying, the…
Acting as a team, twin stem cells activate the immune system to suppress tumor growth and prolong survival in representative preclinical models. Brigham and Women’s…
Researchers at Mass Eye and Ear, part of Mass General Brigham, have successfully used adeno-associated virus vectors in gene therapies to treat genetic hearing loss…
Researchers have developed a “mini gene” therapy for a debilitating syndrome that results in both blindness and deafness. Usher Syndrome type 1F is a rare,…
Researchers from Temple University and UNMC collaborate in a study recently published in the journal Proceedings of the National Academy of Sciences. Gene-editing therapy targeting…
Bacterial Injection System Delivers Proteins in Mice and Human Cells With further development, the programmable system could be used in a range of applications including…
Scientists at St. Jude Children’s Research Hospital have developed a tool that can locate safe places to introduce genes into human DNA. The tool is an…
The patients had Leber Congenital Amaurosis, a type of genetic congenital blindness. According to researchers at the Scheie Eye Institute at the Perelman School of…