Scientists Discover Potential Opioid Replacement for Back Pain
The study indicates that nanocarriers loaded with DNA may serve as alternatives to opioids. Recent research demonstrates that gene therapy delivered by nanocarriers can effectively…
Gene Therapy News
Gene therapy is a medical technique that involves modifying the genes inside an individual’s cells to treat or prevent disease. It allows doctors to treat a disorder by inserting, altering, or removing genes within a patient’s cells instead of using drugs or surgery. Gene therapy can be targeted at somatic (non-reproductive) cells to address conditions like cancer, cystic fibrosis, heart disease, diabetes, and hemophilia, or at germline cells, though the latter is more controversial and heavily regulated due to ethical concerns and the potential for changes to be passed on to future generations.
ZIP7 Protein: New Target for Treating Degenerative Diseases Like Alzheimer’s and Parkinson’s
Researchers have identified a gene therapy target that could potentially slow the development and progression of degenerative diseases. Proteins serve as building blocks, receptors, processors,…
From Theory to Therapy: MIT’s Computational Breakthrough in Protein Optimization
MIT researchers plan to search for proteins that could be used to measure electrical activity in the brain. To engineer proteins with useful functions, researchers…
The Unexpected Key to Safe Gene Therapy: Bird Junk DNA
Retrotransposons can insert new genes into a “safe harbor” in the genome, complementing CRISPR gene editing. The recent greenlighting of a CRISPR-Cas9 treatment for sickle…
Revolutionary Gene Therapy Offers New Hope for Sickle Cell Disease Patients
New findings from a clinical trial, recently published in the New England Journal of Medicine, suggest that stem cell gene therapy could be a potential…
Revolutionary Gene Therapy Tackles Parkinson’s at Its Source: Promising Results in Primates
Scientists from the Shenzhen Institute of Advanced Technology (SIAT) within the Chinese Academy of Sciences (CAS), along with their partners, have designed a targeted gene…
Walking Wonders: Neuron Regeneration Breakthroughs in Spinal Cord Injuries
Guiding cells to natural target region key to functional recovery. In a new study in mice, a team of researchers from the University of California,…
Defying the “Impossible” – Reversing Paralysis Through Spinal Cord Regeneration
Scientists at .NeuroRestore, Switzerland, report in Science that they have developed a gene therapy that was proven in mice to stimulate nerve regrowth across spinal…
Unlocking the Ear’s Backdoor: Unexpected Discovery Opens New Possibilities for Hearing Restoration
An international team of researchers has developed a new method to deliver drugs into the inner ear. This breakthrough was made possible by utilizing the…
Solving the Mystery of Long-Lasting Cancer Treatment – Scientists Reveal New Insights
Researchers from UCL, Great Ormond Street Hospital, and the Wellcome Sanger Institute have unveiled findings that shed light on why certain children experience extended remission…
Resetting the Brain’s Reward Pathway: Gene Therapy’s Breakthrough in Alcohol Addiction
Gene Therapy for Alcohol Use Disorder Gene therapy might offer a one-time, sustained treatment for patients with serious alcohol addiction, also called alcohol use disorder,…
Reversing Hearing Loss – A New Promising Genetic Treatment
Researchers at The Institute of Psychiatry, Psychology & Neuroscience (IoPPN) at King’s College London have successfully reversed hearing loss in mice. Their findings, published in…
A 90% Drop in Drinking: The Power of Gene Therapy in Treating Alcohol Use Disorder
Already used to treat Parkinson’s disease, researchers found surgical treatment dramatically reduced chronic heavy drinking. A form of gene therapy currently used to treat Parkinson’s…
Sodium Power – New Gene Therapy Treats Chronic Pain
Scientists have pinpointed the area where a protein regulates sodium ion channels, and by inserting the channel’s genetic material into a virus, they were able…
Revolution in Pet Sterilization: Gene Therapy Offers Long-Term Contraception for Cats
Research study’s findings offer a potential alternative to surgical spaying. Currently, there are no contraceptives capable of producing permanent sterilization in companion animals. Spaying, the…
New Weapon Against Brain Cancer: Gene Engineered Cell Therapy’s Two-Pronged Assault on Metastatic Melanomas
Acting as a team, twin stem cells activate the immune system to suppress tumor growth and prolong survival in representative preclinical models. Brigham and Women’s…
Gene Therapy Breakthrough in Treatment of Age-Related Hearing Loss
Researchers at Mass Eye and Ear, part of Mass General Brigham, have successfully used adeno-associated virus vectors in gene therapies to treat genetic hearing loss…
Harvard Researchers Design “Mini Gene” Therapy for Severe Genetic Disease
Researchers have developed a “mini gene” therapy for a debilitating syndrome that results in both blindness and deafness. Usher Syndrome type 1F is a rare,…