In experiments with rats, pigs and monkeys, Johns Hopkins Medicine researchers have developed a way to deliver sight-saving gene therapy to the retina. If proved…
Mitochondrial disease is now thought to be the second most commonly diagnosed genetic disease worldwide, and, unfortunately, there are still no proven treatment strategies for…
A team of researchers from Harvard and Mass General Hospital has found a gene therapy that delivers a protein which suppresses the development of female…
In a newly published study, MIT researchers show that a new gene-editing technique, known as CRISPR, can reverse a rare liver disorder caused by a…
Inducing cells to express telomerase, the enzyme which is supposed to slow down the metabolic clock, has enabled researchers boost the lifespan of mouse by…
A Dutch company, uniQure, states that it will start selling the first human gene therapy to be approved in the West by mid-2013. They expect…
A new gene therapy has the ability to fix a defective sense of smell in mice by repairing problems with the cilia on their olfactory…
Researchers at California Institute of Technology (Caltech) believe they have found a way to help the brain replace damaged oligodendrocytes and myelin. By using a…
Researchers from the Perelman School of Medicine at the University of Pennsylvania and the Children’s Hospital of Philadelphia used gene therapy to improve the vision…