New Tool Identifies Safe Places To Introduce Genes Into Human DNA
Scientists at St. Jude Children’s Research Hospital have developed a tool that can locate safe places to introduce genes into human DNA. The tool is an…
Scientists at St. Jude Children’s Research Hospital have developed a tool that can locate safe places to introduce genes into human DNA. The tool is an…
The patients had Leber Congenital Amaurosis, a type of genetic congenital blindness. According to researchers at the Scheie Eye Institute at the Perelman School of…
Researchers discover a new class of drugs that provide leukemia patients with a safer, more targeted form of therapy. Chemotherapy isn’t fun. It’s no secret…
Following treatment, two of the four children’s measurements of cone function closely resembled those of normal-sighted research participants. According to a recent study led by…
The study showed that CRISPR therapeutics can damage the genome. The researchers caution: “The CRISPR genome editing method is very effective, but not always safe….
Positive results from a study on precise medication dosing. According to a recent research conducted by the U.S. Department of Veterans Affairs, pharmacogenomic testing may assist…
Researchers identified 48 genes that are associated with hearing loss, including 10 new variants. Hearing loss is a common problem caused by noise, age, disease,…
New research from the UNC Neuroscience Center lab of Ben Philpot, Ph.D., finds restoring lost gene activity prevents many disease signs in an animal model…
Identifying DNA Repair Genes Holds Promise for Improving Cancer Treatment Cancer is one of the leading causes of death in the United States and worldwide….
In mouse studies, pain-blocking neurotransmitters produced long-lasting benefits without detectable side effects. An international team of researchers led by scientists at the University of California…
University of California San Diego (UCSD) study uses lab-grown human brain tissue to identify neural abnormalities in Pitt-Hopkins Syndrome and test gene therapy tools. In…
Findings could lead to targeted approach for treating aging. Research from the Babraham Institute has developed a method to ‘time jump’ human skin cells by…
First approach to promote electrical excitation of heart cells in live mammals could lead to new gene therapy treatments for a wide range of heart…
Researchers at Harvard’s Wyss Institute, Harvard Medical School, and the ETH Zurich predict and validate genomic safe harbors for therapeutic genes, enabling safer, more efficient,…
Novel obesity treatments such as modulation of the gut microbiome and gene therapy are underutilized and could help fight the obesity epidemic, according to a…
A compact and efficient CRISPR-Cas system, named CasMINI, could be broadly useful for cell-engineering and gene-therapy applications because it is easier to deliver into cells….
Bioengineers have repurposed a “non-working” CRISPR system to make a smaller version of the genome engineering tool. Its diminutive size should make it easier to…
Mount Sinai researchers have developed a therapeutic agent that shows high effectiveness in vitro at disrupting a biological pathway that helps cancer survive, according to…